FAST AS CSF Collection Study Community Presentation
Join Biogen’s AS CSF Collection Study to investigate UBE3A protein as a biomarker for Angelman syndrome. Open for enrollment until August 2021. Learn more and get involved.
Roche Genentech Webinar
Join Roche and Genentech’s webinar to learn about their Angelman Syndrome program, updates on the FREESIAS study, and the Phase 1 TANGELO study. Stay informed and engaged!
Warrior Families: Advancing Regenerative Medicine Through Science
Join the Warrior Families webinar by the FDA’s Office of Therapeutic Products, focusing on the role of families in advancing regenerative medicine for rare diseases. Learn from experts, engage in Q&A, and explore patient-centered approaches.
A Joint Community Webinar with Dr. Berry-Kravis on Roche updates
Join our webinar with Dr. Berry-Kravis discussing Roche updates, TANGELO study, and future research. Learn about trial logistics, patient care, and lessons learned from setbacks.
Angelman Updates with Dr. Terry Jo Bichell, featuring Dr. Yong-Hui Jiang
Explore Dr. Yong-Hui Jiang’s groundbreaking work on Angelman Syndrome, from identifying the UBE3A gene to creating brain organoids for disease study and treatment testing. Discover hope for future advancements.
Angelman Updates with Dr. Terry Jo Bichell, featuring Dr. Ralf Schmid
Join Dr. Terry Jo Bichell as she interviews Dr. Ralf Schmid on his groundbreaking work in gene therapy for Angelman Syndrome. Discover the potential of this innovative treatment in improving lives.
Angelman Updates with Dr. Terry Jo Bichell, featuring Dr. Joe Anderson
Explore Dr. Joe Anderson’s unique approach to genetic therapy for Angelman Syndrome, using patient’s own stem cells and immune system. Promising results in animal models, moving towards clinical trials.
Angelman Updates with Dr. Terry Jo Bichell, featuring Dr. Jim Wilson
Explore the latest Angelman Syndrome research with Dr. Jim Wilson, discussing gene therapy, antisense oligonucleotides, and genome editing. Discover the future of treatments and collaborations in rare disease research.
Angelman Updates with Dr. Terry Jo Bichell, featuring Dr. David Segal
Join Dr. Terry Jo Bichell as she interviews Dr. David Segal on his groundbreaking Angelman Syndrome research. Discover the power of collaboration and the promising future of therapeutics.
Angelman Updates with Dr. Terry Jo Bichell, featuring Dr. Christy Zigler
Explore Angelman Updates with Dr. Terry Jo Bichell, featuring Dr. Christy Zigler’s research on the ORCA measure for assessing communication abilities in Angelman Syndrome patients.