FAST Roadmap to a C.U.R.E. 2.0 Join Allyson Berent at the 2022 FAST Science Summit as she discusses the roadmap to a C.U.R.E. 2.0 for Angelman Syndrome and the science behind it. Be part of the movement!
Fireside Chat: The FAST Commercial Philosophy Join Alana Newhouse and Ryan Jacob as they discuss FAST’s commercial philosophy, the importance of partnerships, and the challenges in the rare disease community. Discover the balance between communication and commercialization.
NNZ-2591 as a Treatment for Angelman Syndrome Explore the potential of NNZ-2591 as a treatment for Angelman syndrome. Learn about Neuren Pharmaceuticals’ clinical trials, preclinical studies, and the drug’s neurobiological properties.
PTC-AS Gene Therapy Program Update Get the latest update on PTC Therapeutics’ PTC-AS gene therapy program. Discover their innovative treatments for rare disorders, recent approvals, and future plans for Angelman syndrome patients.
Pharma Panel Discussion and Audience Q&A Join the 2022 FAST Science Summit’s Pharma Panel Discussion on Angelman Syndrome. Gain insights on treatment options, drug development, and patient advocacy from leading experts. Stay engaged and hopeful for the future.
Rapidly Evolving Opportunities for Treatments for Rare Genetic Diseases Explore the rapidly evolving opportunities for treatments for rare genetic diseases with Dr. Wendy Chung at the 2022 FAST Science Summit. Discover the importance of early diagnosis, genomics, and precision medicine.
Researchers Panel Discussion and Audience Q&A Join the 2022 FAST Science Summit’s panel discussion on Angelman syndrome research and treatment. Hear from experts addressing audience questions and sharing insights on future developments.
Roche Angelman Syndrome Program Update – 2022 Get the latest updates on Roche’s Angelman Syndrome program, including the progress of Rugonersen, TANGELO Phase 1 drug study, PET imaging study, and the introduction of Alogabat.
The Importance of Patient Input for Coverage and Payment of New Therapies Explore the importance of patient input in coverage and payment of new therapies with experts Sarah Pitluck and John Jarvis. Learn about pricing strategies, patient advocacy, and the role of surveys in improving access to treatments.
Update on Progress Around the World from FAST Global Get the latest updates on FAST Global’s progress in accelerating the mission to cure Angelman Syndrome. Learn about their initiatives, collaborations, and achievements worldwide.
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