Genetic Approaches for Treating Angelman Syndrome Explore the latest genetic approaches to treat Angelman Syndrome, including gene therapy, genome editing, and RNA interference. Learn about the challenges, clinical trials, and future directions.
Ionis Pharmaceuticals Angelman Syndrome Program Update Explore Ionis Pharmaceuticals’ progress in their Angelman Syndrome program, including a clinical trial initiation, collaborations for research, and an introduction to the Halos trial. Stay updated with the latest developments.
Panel Discussion with Pharma Get the latest updates on clinical trials for Angelman Syndrome from the 2021 FAST Science Summit. Learn about trial progress, patient selection, drug access, and future plans from leading pharma representatives.
Panel Discussion with Researchers Explore key insights from the 2021 FAST Science Summit panel discussion, where experts discuss advancements and potential treatments for Angelman syndrome, a rare genetic disorder.
Putting Patients at the Center Explore Taysha Gene Therapies’ approach to developing treatments for rare neurological diseases, their partnership with UT Southwestern, and their commitment to patient-centered care.
Stem Cell and Gene Therapy Platforms Explore the latest advancements in stem cell and gene therapy platforms with Jan A. Nolta at the 2021 FAST Science Summit. Discover ongoing research, clinical trials, and future directions at UC Davis.
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